Curative Therapies for Bone Marrow Failure
Bone marrow failure in children arises either from immune dysregulation or genetic predisposition. The advent of readily available germline and somatic genetic platforms now allow…
Course Instructor: Timothy S. Olson, MD, PhD
Curative and Emerging Therapies for Sickle Cell Disease
For decades, treatment options for patients suffering from chronic, severe manifestations of sickle cell disease have been limited to hydroxyurea therapy and chronic red blood…