At the end of this session, learners will be able to describe an overview of spinal muscular atrophy (SMA) including 5q and non-5q SMA, review diagnosis, classification, genetic basis and pathophysiology of SMA, discuss the three FDA approved disease modifying therapies for SMA and trial data, and address current clinical care and monitoring of SMA.
This seminar focuses on neurology and was delivered at the Open Medical Institute in Salzburg, Austria, from February 20 – 26, 2022.
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