The Safe and Effective Practice of AAV Gene Therapy
Join the Clinical In Vivo Gene Therapy (CIGT) team at Children’s Hospital of Philadelphia for an exciting educational symposium, as we provide fundamental knowledge on…
Join the Clinical In Vivo Gene Therapy (CIGT) team at Children’s Hospital of Philadelphia for an exciting educational symposium, as we provide fundamental knowledge on…
Primary mitochondrial diseases share in common an impaired ability to generate energy. Highly heterogeneous in etiology and phenotypes, primary mitochondrial diseases are collectively the most…